Yintoni injongo yoPhononongo lwe-STEER?

Injongo yoPhononongo lwe-STEER kukuqonda enoba unyango oluphandwayo lwemfuza i-OAV101 lukhuselekile kwaye lunganceda na ekuphuculeni ukusebenza kwezihlunu ebantwaneni abaneminyaka emi-2 ukuya kwengaphantsi kweli-18 abanee-SMA yoDidi lwesi-2.

Ngubani onokujoyinga?

Yintoni i-OAV101?

I-OAV101 lunyango lwemfuza olwenzelwe ukuhambisa ikopi entsha esebenzayo yemfuza ye-SMN1 iye kwimithambo-luvo yentshukumo. Injongo kukuba imfuza entsha ye-SMN1 yenze iprotheni ye-SMN eyoneleyo ukuze kuthintelwe ukuphulukana nangakumbi nemithambo-luvo yentshukumo.

Ngubani onokuthatha inxaxheba kuphononongo?

Uphononongo lolwabantwana abaneminyaka emi-2 ukuya kwengaphantsi kweli-18 abane-SMA yoDidi lwesi-2 aba:

  • Abakwaziyo ukuzihlalela ngaphandle koncedo kodwa abangazange bakhe bazihambela ngaphandle koncedo.
  • Abaqale ukubonisa iimpawo ze-SMA ebudaleni obungangeenyanga ezi-6 okanye ngaphazulu.
  • Abangekafumani naluphi unyango olonyusa i-SMN.